Swiss drugmaker Novartis said on Monday its gene therapy helped improve motor function in children with a rare muscle ...

Amyotrophic lateral sclerosis (ALS) is a serious and usually fatal neurodegenerative disorder in which motor neurons deteriorate and die. | Genetics And Genomics ...

Recent research has found a connection between a Parkinson's disease gene and changes in speech. The study revealed that the ...

Novartis’ Phase III study has demonstrated significant improvement in motor function in children and young adults with spinal ...

Gene Therapy, the Weizmann scientists present an innovative genetic treatment for Gaucher disease that has shown promising results in mice, including dramatically increasing life span and preserving ...

"It is important for families to understand the genetic basis of these disorders, due to the frequency ... and deficits in learning, memory and motor impairment. "We found most GTF3C3 mutations ...

Topline data were announced from a phase 3 trial evaluating intrathecal onasemnogene abeparvovec (OAV101 IT), an investigational gene therapy ... Functional Motor Scale – Expanded (HFMSE ...

Capsida Biotherapeutics has unveiled data showing that its AAV-delivered gene therapy for developmental ... corrected cognitive and motor deficits and reduced seizures in mice up to one year ...

Dyslexia is a common learning difficulty in which genes often play a role. How do genes associated with dyslexia relate to brain structure in the general population? In a large-scale study, a team of ...