These treat conditions like hypertrophic cardiomyopathy, and intractable epilepsy. China’s National Healthcare Security ...

After Natalie Rex was diagnosed with Friedreich’s ataxia -- a rare genetic and usually fatal neurological disease -- her twin ...

India is streamlining access to rare disease drugs by waiving local clinical trials for some medications. The drug regulator ...

In the U.S., about 30 million people—half of them children—have a rare disease, according to the U.S. Government ...

Innovations in rare blood disorders took center stage at the 2024 American Society of Hematology (ASH) Annual Meeting & ...

Get your daily dose of health and medicine every weekday with STAT’s free newsletter Morning Rounds. Sign up here. Good ...

MALVERN, PA — Ocugen, Inc. (NASDAQ: OCGN) has announced that Dr. Shankar Musunuri, Chairman, CEO, and Co-Founder, will ...

The family of a 6-year-old girl from Apex with severe aplastic anemia is hoping to find a match for a bone marrow donor for ...

As part of this effort, the NHSA has adjusted the national medical insurance catalog for seven consecutive years since its ...

A DeKalb County police officer suffering from suffering from a rare kidney disease is in a race against time. Here's how you ...

India, home to 96 million rare disease patients, is considering eliminating local drug trials to expedite treatments, raising ...

NEW YORK, Dec. 03, 2024 (GLOBE NEWSWIRE) -- Know Rare, a global support platform for people impacted by rare disease and rare ...